If approved, DTX401 will be the first therapy approved to treat the underlying cause of GSDIaNOVATO, Calif., Dec. 30, 2025 ...

Ultragenyx Pharmaceutical ( ($RARE) ) just unveiled an update. On December 30, 2025, Ultragenyx Pharmaceutical announced it had completed the ...

Ultragenyx jumps after completing rolling BLA submission to the FDA for DTX401, an AAV gene therapy that could become the first approved treatment for GSDIa.

Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE) today announced that it has completed the rolling submission of its Biologics License Application (BLA) ...

The increasing prevalence of diabetes has focused interest on practical dietary practices that can help ensure stable levels ...

According to the health expert, the human body has the most efficient detox system ever: the liver, kidneys, lungs, gut, and ...

Shares in Ultragenyx and Mereo BioPharma have plunged after their drug for osteogenesis imperfecta (OI) or brittle bone ...

A new study reveals how artificial sweeteners like sorbitol can impact liver health, potentially leading to steatotic liver ...

A simple blend with spinach, banana, berries, and yogurt or plant milk is becoming one of the most effective recovery tools ...

Three years after the diagnosis that would change his life Mat speaks openly about the ordeal. "I felt unstoppable," he says.

Self-control—or the ability to manage one's impulses, emotions, and behaviors to achieve long-term goals—is what separates humans from the rest of the animal kingdom. Self-control is primarily rooted ...